About the Center: The goals of the Gene Therapy Program, to develop and commercialize transformative genetic-based therapeutics, are driven by the unmet needs of patients with inherited genetic diseases.
Achievements: The services of the PCM are:
- Rapid animal model development, expert validation and support collaboration for discovery and preclinical development and validation of novel therapies
- High standard of animal welfare and regulatory compliance
- High quality animal care and husbandry for laboratory animals
- Colony breeding, expansion and maintenance of genetically engineered rodent models
- Advanced imaging technologies
- Neurobehavioral and motor function technologies
- Surgical services to support model development
- Specialized dosing procedures to support research and IND-enabling studies
Address: Suite 2000 Translational Research Labs (TRL)
125 S. 31st Street
Philadelphia, PA 19104-3403
Phone: (215) 898-0226
Web Site: https://gtp.med.upenn.edu
