About the Center: MMG‘s unwavering mission is to remain a leader in genetics and microbiology research, and to provide excellence in teaching and mentoring at all educational levels. MMG maintains strong, diverse research programs and plays a significant role in the educational missions of the School of Medicine. Our goal is to continue to foster…
About the Center: The Center for Cell and Gene Therapy at Baylor College of Medicine, Texas Children’s Hospital, and Houston Methodist Hospital provides an infrastructure to rapidly translate novel cell and gene therapy protocols from the laboratory to the clinic. The comprehensive approach of the center brings a wide variety of scientists and clinicians together…
About the Center: Clinical trial success in a few gene therapy trials for inherited disorders, including one form of early onset retinal degeneration, has led to validation of the adeno-associated viral vector (AAV) platform. While AAV has several desirable properties and has proven safe and efficacious in these studies, several limitations of the vector system…
About: Helping children and young people live their healthiest lives possible. Each year our services manage: 51,000 inpatient admissions 92,000 Emergency Department presentations Over one million outpatient service visits Our vision and mission: The formation of the Network in 2010 was a significant milestone for paediatric services in NSW. The Network’s leadership group has established a solid corporate and strategic platform to enhance…
About the Center: The Powell Gene Therapy Center (PGTC) at the University of Florida has been instrumental in the development of newer, safer agents for the delivery of therapeutic genes to patients with genetic diseases, such as cystic fibrosis (CF) and alpha 1-antitrypsin deficiency (AAT-D). New programs will extend the use of the harmless virus, called…
About the Center: The Mathews Center for Cellular Therapy (MCCT) at downtown Chicago’s Northwestern Memorial Hospital offers researchers, clinicians and biotech companies regulatory compliant labs and services to manufacture minimally manipulated and complex biotechnology products. Achievements: Northwestern’s adult stem cell, solid organ transplant programs, and allergy and immunology divisions The Robert and Ann Lurie Children’s…
About: The department of Pharmaceutical Gene Modulation (PGM) is focused on the development of drugs for the therapeutic manipulation of gene activity. Genetic medicines and delivery forms are being developed for the specific and efficient treatment of different diseases. Currently, the research is focused on cancer and inflammatory diseases. Achievements: Patients with Parkinson’s disease are…
About: IRCCS Ospedale San Raffaele is one of the leading research institutes in Italy as per volume and quality of scientific output. Since 2001, San Raffaele has been recognized by the Italian Ministry of Health as a research hospital (Istituto di Ricovero e Cura a Carattere Scientifico, IRCCS) with the speciality of Molecular Medicine. This…
About: In 2016, our name changed to the UCL Great Ormond Street Institute of Child Health. The inclusion of ‘Great Ormond Street’, is to reflect our close and strong partnership with Great Ormond Street Hospital, whilst continuing to be faithful to our mission to improve all of child health. In everything we do, we try…
About the Center: Nationwide Children’s Hospital is a primary pediatric hospital in Columbus, Ohio, with more than 1,316 medical staff members and over 11,200 total employees. In recent years, the hospital has been ranked as one of America’s Best Children’s Hospitals by US News & World Report. It is also the pediatric teaching hospital for The Ohio State University College of Medicine.…